Gene therapy

特許 権利維持 Gene therapy is the use of nucleic acid polymers as a drug to treat disease by therapeutic delivery into a patient's cells, where they are either expressed as proteins, interfere with the expression of proteins, or possibly even correct genetic mutations. The most common form of gene therapy involves using DNA that encodes a functional, therapeutic gene to replace a mutated gene. In gene therapy, the nucleic acid molecule is packaged within a "vector", which is used to get the molecule inside cells within the body.